Disease Landscape and Forecast Insights
Comprehensive market intelligence and actionable insights help you optimize your long-term disease strategy
Rare Diseases and Orphan Drugs – Access & Reimbursement – Access & Reimbursement – Gene Therapies for Rare Diseases (US)
Given the availability of an increasing number of approved innovative, high-cost gene therapies, value assessment and novel approaches to reimbursement are rapidly gaining importance. To assist…
Gene Therapies for Rare Diseases | Disease Landscape & Forecast | US/EU5/Japan | 2022
Approximately 80% of rare diseases have a genetic etiology. Gene therapies have the potential to transform the treatment of rare diseases and may provide a functional cure for some. However, these…
Gene Therapies for Rare Diseases | Disease Landscape & Forecast | US/EU5/Japan | 2021
Approximately 80% of rare diseases have a genetic etiology. Gene therapies hold the potential to transform the treatment of rare diseases and may provide a functional cure for some. However, these…