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Rare Disease Innovation – Navigating Capital, Complexity, and Clinical Opportunity
Speakers
This moderated panel brings together leading investors and entrepreneurs at the forefront of rare disease innovation to explore the critical tension between abundance and scarcity—abundant capital and investor appetite for orphan indications, but scarcity of patients for recruitment, scarcity of validated biomarkers for proof-of-concept, and scarcity of regulatory precedent for next-generation modalities like gene therapies and precision protein degradation.
Watch now to gain hard-won insights from these leading experts on:
- Capital allocation strategies
- Portfolio construction
- Patient engagement imperatives
- The regulatory strategies required to advance therapies from concept to clinic and beyond
