Disease Landscape and Forecast Insights
Comprehensive market intelligence and actionable insights help you optimize your long-term disease strategy
- 1
- 2
Rare Diseases and Orphan Drugs – Landscape & Forecast – Disease Landscape & Forecast (G7)
Approximately 80% of rare diseases have a genetic etiology. Gene therapies have the potential to transform the treatment of rare diseases and, in some cases, provide a functional cure. However,…
Rare Diseases and Orphan Drugs – Access & Reimbursement – Access & Reimbursement – Gene Therapies for Rare Diseases (US)
Given the availability of an increasing number of approved innovative, high-cost gene therapies, value assessment and novel approaches to reimbursement are rapidly gaining importance. To assist…
Rare Diseases and Orphan Drugs | Disease Landscape & Forecast | Gene Therapies | G7 | 2020
Approximately 80% of rare diseases have a genetic etiology. Gene therapies hold the potential to transform the treatment of rare diseases and may provide a functional cure for some. However, these…
Rare Diseases and Orphan Drugs – Access & Reimbursement – Rare Diseases and Orphan Drugs – Top Five European Markets
MARKET OUTLOOK Progress in R&D and technology, regulatory and monetary incentives for advancing the development of rare diseases treatment, and ongoing industry focus are key drivers of growth in…
Rare Diseases and Orphan Drugs | Disease Landscape & Forecast | Gene Therapies | G7 | 2019
Approximately 80% of rare diseases have a genetic etiology. Gene therapies hold the potential to transform the treatment of rare diseases and may provide a functional cure for some. However, these…
Idiopathic Pulmonary Fibrosis | Niche & Rare Disease Landscape & Forecast | US/EU5 | 2019
MARKET OUTLOOK Progress in R&D and technology, regulatory and monetary incentives for advancing the development of treatments for rare diseases, and ongoing focus by the pharmaceutical market…
Rare Disease and Orphan Drugs | Special Topics | US | Partnering with Patient Advocacy Groups to Accelerate Orphan Drug Development | 2018
Patient advocacy groups play many roles in orphan drug development, including funding and propelling early development and interacting with key stakeholders such as the patients, their caregivers,…
- 1
- 2
