Approximately 80% of rare diseases have a genetic etiology. Gene therapies have the potential to transform the treatment of rare diseases and may provide a functional cure for some. However, these innovative treatments must come with equally innovative programs to optimize access in a global healthcare market that is still grappling with how to fairly assess their value and absorb their higher upfront costs. Nonetheless, the pipeline for gene therapies is burgeoning, as large pharmaceutical companies (e.g., Pfizer, Roche, Novartis) assume increasing stakes in this arena. In this content, we will explore the clinical and commercial potential of gene therapies in key therapeutic areas (i.e., neurology, ophthalmology, and hematology).
QUESTIONS ANSWERED
GEOGRAPHIES
United States, EU5, Japan
PRIMARY RESEARCH
More than 25 country-specific interviews with thought-leading neurologists, ophthalmologists, and hematologists. Supported by survey data collected for this and other Clarivate research.
EPIDEMIOLOGY
Diagnosed prevalent and/or incident patient populations eligible for gene therapies in covered indications.
FORECAST
10-year, annualized, drug-level sales and patient share of key gene therapies through 2031, segmented by brands / generics, geography, and key indications.
EMERGING THERAPIES
Pipeline gene therapy coverage for select indications across therapy areas.
PRODUCT DESCRIPTION
Disease Landscape & Forecast provides comprehensive market intelligence with world-class epidemiology, keen insight into current treatment paradigms, in-depth pipeline assessments, and drug forecasts supported by detailed primary and secondary research.
SOLUTION ENHANCEMENT
Disease Landscape & Forecast will feature continual updates to provide timely insights and analyses as meaningful indication-specific news and events unfold.