{"id":573635,"date":"2025-12-18T08:09:16","date_gmt":"2025-12-18T08:09:16","guid":{"rendered":"https:\/\/clarivate.com\/life-sciences-healthcare\/?p=571602"},"modified":"2026-01-23T09:02:18","modified_gmt":"2026-01-23T09:02:18","slug":"understanding-the-epidemiology-of-sma","status":"publish","type":"post","link":"https:\/\/clarivate.com\/life-sciences-healthcare\/ko\/blog\/understanding-the-epidemiology-of-sma\/","title":{"rendered":"\ucc99\ucd94\uc131\uadfc\uc704\ucd95\uc99d \uc5ed\ud559\uc5d0 \ub300\ud55c \uc774\ud574"},"content":{"rendered":"<p>\ucc99\uc218\uc131\uadfc\uc704\ucd95\uc99d(Spinal Muscular Atrophy, SMA)\uc740 \ucc99\uc218 \ub0b4 \uc54c\ud30c \uc6b4\ub3d9\uc2e0\uacbd\uc138\ud3ec\uac00 \uc810\uc9c4\uc801\uc73c\ub85c \uc190\uc0c1\ub418\uba74\uc11c \uadfc\uc721 \uc57d\ud654\uc640 \uc704\ucd95\uc774 \uc9c4\ud589\ub418\ub294 \ud76c\uadc0 \uc720\uc804 \uc9c8\ud658\uc785\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ube14\ub85c\uadf8 \uae00\uc740 \uc5ec\ub7ec \uc9c0\uc5ed\uc5d0\uc11c \uc218\uc9d1\ud55c \uc720\ubcd1\ub960 \ub370\uc774\ud130\ub97c \ubc14\ud0d5\uc73c\ub85c \uc218\ud589\ud55c \uad11\ubc94\uc704\ud55c \uc5ed\ud559 \ubd84\uc11d\uc744 \ub2e4\ub8e8\uace0 \uc788\uc73c\uba70, \uc9c1\uc811\uc801\uc778 \ub370\uc774\ud130\uac00 \ud655\ubcf4\ub418\uc9c0 \uc54a\uc740 \uacbd\uc6b0\uc5d0\ub294 \ub300\ub9ac \uc778\uad6c(proxy population)\ub97c \ud65c\uc6a9\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774\ubc88 \uc5f0\uad6c\uc758 \ubaa9\uc801\uc740 \uace0\uac00 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc811\uadfc\uc131\uc744 \ud3ec\ud568\ud574, \uc720\uc804\uc801 \uc694\uc778, \uc758\ub8cc \ud658\uacbd, \uc0ac\ud68c\uacbd\uc81c\uc801 \uc694\uc778\uc774 \uacb0\ud569\ub418\uc5b4 \uc804 \uc138\uacc4 SMA \uc720\ubcd1\ub960\uc774 \uc5b4\ub5bb\uac8c \ud615\uc131\ub418\ub294\uc9c0\ub97c \uc0b4\ud3b4\ubcf4\ub294 \ub370 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<h3><strong>\uc9c0\uc5ed\ubcc4 \uc720\ubcd1\ub960\uc758 \ucc28\uc774<\/strong><\/h3>\n<p>\uc804 \uc138\uacc4 \ub370\uc774\ud130\ub97c \ubd84\uc11d\ud55c \uacb0\uacfc, SMA\uc758 \uc9c4\ub2e8 \uc720\ubcd1\ub960\uacfc \uc544\ud615(subtype) \ubd84\ud3ec\ub294 \uc9c0\uc5ed\ubcc4\ub85c \uc720\uc758\ubbf8\ud55c \ucc28\uc774\ub97c \ubcf4\uc600\uc2b5\ub2c8\ub2e4. \uc720\ub7fd\uc758 \uacbd\uc6b0, SMA \uce58\ub8cc \ud658\uacbd\uc774 \uc720\uc0ac\ud558\ub2e4\ub294 \uc810\uc744 \uace0\ub824\ud574 EU5 \uad6d\uac00\uc758 \ud3c9\uade0 \ub370\uc774\ud130\ub97c \ud65c\uc6a9\ud558\uc5ec \uc624\uc2a4\ud2b8\ub9ac\uc544\uc640 \uc2a4\uc704\uc2a4\uc758 SMA 1\ud615 \ubc0f 2\ud615 \uc720\ubcd1\ub960\uc744 \uce58\ub8cc\uc81c \ud22c\uc5ec \ud658\uc790 \ube44\uc911\uc5d0 \ub9de\ucdb0 \uc870\uc815\ud588\uc2b5\ub2c8\ub2e4.\ub77c\ud2f4\uc544\uba54\ub9ac\uce74(LATAM)\uc5d0\uc11c\ub294 \uc544\ub974\ud5e8\ud2f0\ub098, \ube0c\ub77c\uc9c8, \ucf5c\ub86c\ube44\uc544 \ub4f1 \uad6d\uac00\ubcc4\ub85c SMA \uc544\ud615\ubcc4 \uc720\ubcd1\ub960\uc774 \uc11c\ub85c \ub2e4\ub974\uac8c \ubcf4\uace0\ub418\uc5c8\uc2b5\ub2c8\ub2e4.\uc544\uc2dc\uc544\u00b7\ud0dc\ud3c9\uc591(APAC) \uc9c0\uc5ed\uc5d0\uc11c\ub294 \ud64d\ucf69, \uc2f1\uac00\ud3ec\ub974\uc640 \uac19\uc740 \uace0\uc18c\ub4dd \uad6d\uac00\uac00 \uc778\ub3c4\ub124\uc2dc\uc544, \ubca0\ud2b8\ub0a8 \ub4f1 \uc0c1\ub300\uc801\uc73c\ub85c \uc800\uc18c\ub4dd \uad6d\uac00\uc640\ub294 \ub2e4\ub978 \uc720\ubcd1\ub960 \uc591\uc0c1\uc744 \ubcf4\uc600\uc2b5\ub2c8\ub2e4. \uc544\ud504\ub9ac\uce74, \uc911\ub3d9, \uc544\uc2dc\uc544 \uc544\ub300\ub959 \uc9c0\uc5ed\uc5d0\uc11c\ub294 \uc774\uc9d1\ud2b8, \uc778\ub3c4, \uc0ac\uc6b0\ub514\uc544\ub77c\ube44\uc544\uc640 \uac19\uc740 \uad6d\uac00\ub4e4\uc774 \uc720\uc804\uc801 \ud2b9\uc131, \uc758\ub8cc \uc2dc\uc2a4\ud15c, \uc0ac\ud68c\uacbd\uc81c\uc801 \uc694\uc778\uc758 \uc601\ud5a5\uc744 \ubc1b\uc544 \uac01\uae30 \ub2e4\ub978 \uc720\ubcd1\ub960 \ud328\ud134\uc744 \ub098\ud0c0\ub0c8\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774\ud6c4 SMA \uc720\ubcd1\ub960\uc5d0 \uc601\ud5a5\uc744 \ubbf8\uce58\ub294 \uc8fc\uc694 \uc694\uc778\uc744 \ubcf4\ub2e4 \uc2ec\uce35\uc801\uc73c\ub85c \ubd84\uc11d\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<ul>\n<li>\n<h3><strong>\uc720\uc804\uc801 \uc694\uc778: \ud558\ub514\u2013\ubc14\uc778\ubca0\ub974\ud06c \ud3c9\ud615\uc758 \uc5ed\ud560<\/strong><\/h3>\n<\/li>\n<\/ul>\n<p>SMA\ub294 \uc0c1\uc5fc\uc0c9\uccb4 \uc5f4\uc131(autosomal recessive) \ubc29\uc2dd\uc73c\ub85c \uc720\uc804\ub418\ub294 \uc9c8\ud658\uc785\ub2c8\ub2e4. \uc774\uc5d0 \ub530\ub77c \ubcf8 \ubd84\uc11d\uc5d0\uc11c\ub294 \ud558\ub514\u2013\ubc14\uc778\ubca0\ub974\ud06c \ud3c9\ud615(Hardy\u2013Weinberg equilibrium)\uc774\ub77c\ub294 \ud575\uc2ec \uc720\uc804 \uc6d0\ub9ac\ub97c \uc801\uc6a9\ud588\uc2b5\ub2c8\ub2e4. \uc774 \uc774\ub860\uc740 \uc790\uc5f0\uc120\ud0dd\uc774 \uc5c6\uace0, \uc778\uad6c \uc774\ub3d9\uc774 \uac70\uc758 \uc5c6\uc73c\uba70, \uc9d1\ub2e8 \uaddc\ubaa8\uac00 \ucda9\ubd84\ud788 \ud06c\uace0, \ub3cc\uc5f0\ubcc0\uc774\uac00 \ubc1c\uc0dd\ud558\uc9c0 \uc54a\ub294\ub2e4\ub294 \uac00\uc815\uc744 \uc804\uc81c\ub85c \ud569\ub2c8\ub2e4.<\/p>\n<p>\uc774\ub7ec\ud55c \uc870\uac74\uc744 \ubc14\ud0d5\uc73c\ub85c \uc720\uc804\uc801 \ubc30\uacbd\uc774 \uc720\uc0ac\ud55c \ub300\ub9ac \uc778\uad6c(proxy population)\ub97c \uc120\uc815\ud574 \ubcf4\ub2e4 \uc815\ud655\ud55c \uc720\ubcd1\ub960 \ucd94\uc815\uc744 \uc2dc\ub3c4\ud588\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4 \uc720\ub7fd\uc5d0\uc11c\ub294 \uc624\uc2a4\ud2b8\ub9ac\uc544, \ubca8\uae30\uc5d0, \uc2a4\uc704\uc2a4\uc640 \uac19\uc740 \uad6d\uac00\ub4e4\uc774 \uc720\uc0ac\ud55c \uc720\uc804\uc801 \ud2b9\uc131\uc744 \uc9c0\ub2cc \uc9c0\uc5ed\uc744 \ub300\ud45c\ud558\ub294 \ub300\ub9ac \uc9d1\ub2e8\uc73c\ub85c \ud65c\uc6a9\ub418\uc5c8\uc2b5\ub2c8\ub2e4.<\/p>\n<ul>\n<li>\n<h3><strong>\uc758\ub8cc \uc2dc\uc2a4\ud15c: \uacb0\uc815\uc801\uc778 \uc601\ud5a5 \uc694\uc778<\/strong><\/h3>\n<\/li>\n<\/ul>\n<p>\uc758\ub8cc \uc2dc\uc2a4\ud15c\uc774 \ubc1c\ub2ec\ud558\uace0 \uac80\uc9c4 \ubc0f \uc9c4\ub2e8(screening\/detection) \ube44\uc728\uc774 \ub192\uc740 \uc9c0\uc5ed\uc77c\uc218\ub85d SMA \uc720\ubcd1\ub960 \ucd94\uc815\uc5d0 \ud65c\uc6a9\ud560 \uc218 \uc788\ub294 \ub370\uc774\ud130\uac00 \ub354 \ub9ce\uc774 \ubcf4\uace0\ub418\ub294 \uacbd\ud5a5\uc744 \ubcf4\uc600\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4 \uc0ac\uc6b0\ub514\uc544\ub77c\ube44\uc544\ub294 \uc911\ub3d9 \uc9c0\uc5ed \ub0b4 \ub2e4\ub978 \uad6d\uac00\ub4e4\uc5d0 \ube44\ud574 \ubcf4\ub2e4 \uc120\uc9c4\ud654\ub41c \uc758\ub8cc \uc2dc\uc2a4\ud15c\uacfc \ub192\uc740 \uac80\uc9c4\u00b7\uc9c4\ub2e8\uc728\uc744 \uac16\ucd94\uace0 \uc788\uc5b4, SMA \uad00\ub828 \ub370\uc774\ud130\uac00 \uc0c1\ub300\uc801\uc73c\ub85c \ud48d\ubd80\ud569\ub2c8\ub2e4.<\/p>\n<p>SMA \uce58\ub8cc \ubd84\uc57c\uc5d0\uc11c\ub294 \ud601\uc2e0\uc801\uc778 \ubc1c\uc804\uc774 \uc774\ub8e8\uc5b4\uc84c\uc2b5\ub2c8\ub2e4. \ud604\uc7ac SMA \uce58\ub8cc\ub97c \uc704\ud55c \ub450 \uac00\uc9c0 \ud6a8\uacfc\uc801\uc778 \uce58\ub8cc \uc635\uc158\uc774 \uc874\uc7ac\ud558\uba70, \uc774\ub4e4\uc740 \uc791\uc6a9 \uae30\uc804\uacfc \ud22c\uc5ec \ubc29\uc2dd\uc5d0\uc11c \ucc28\uc774\ub97c \ubcf4\uc785\ub2c8\ub2e4.<\/p>\n<p>\ud558\ub098\ub294 \ucc99\uc218\uac15 \ub0b4 \uc8fc\uc0ac\ub85c \ud22c\uc5ec\ub418\ub294 \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(antisense oligonucleotide) \uce58\ub8cc\uc81c\uc774\uba70, \ub2e4\ub978 \ud558\ub098\ub294 \uacbd\uad6c \ud22c\uc5ec\uac00 \uac00\ub2a5\ud55c \uc18c\ubd84\uc790 \uce58\ub8cc\uc81c\ub85c, \ucc99\uc218\uac15 \ub0b4 \uc8fc\uc0ac\uac00 \uc5b4\ub824\uc6b4 \ud658\uc790\ub4e4\uc5d0\uac8c \ubcf4\ub2e4 \uc6a9\uc774\ud55c \uce58\ub8cc \uc635\uc158\uc73c\ub85c \ud3c9\uac00\ub429\ub2c8\ub2e4. \ub450 \uce58\ub8cc\ubc95 \ubaa8\ub450 SMN2 \uc720\uc804\uc790\ub97c \ud45c\uc801\uc73c\ub85c SMN \ub2e8\ubc31\uc9c8 \ubc1c\ud604\uc744 \uc99d\uac00\uc2dc\ud0a4\ub294 \ubc29\uc2dd\uc744 \ud65c\uc6a9\ud574 \uadfc\uc721 \ubc0f \uc2e0\uacbd \uae30\ub2a5 \uac1c\uc120\uc5d0 \uae30\uc5ec\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc774\uc640 \ud568\uaed8 \uae30\ub2a5\uc801\uc778 SMN1 \uc720\uc804\uc790\ub97c \uc6b4\ub3d9\uc2e0\uacbd\uc138\ud3ec\uc5d0 \uc804\ub2ec\ud558\ub294 \uc720\uc804\uc790 \uce58\ub8cc\ub3c4 \uc0ac\uc6a9\ub418\uace0 \uc788\uc73c\uba70, \uc774\ub294 SMA\uc758 \uc720\uc804\uc801 \uadfc\ubcf8 \uc6d0\uc778\uc744 \uc9c1\uc811\uc801\uc73c\ub85c \ud574\uacb0\ud558\ub294 \uc811\uadfc\ubc95\uc785\ub2c8\ub2e4. \uc720\uc804\uc790 \uce58\ub8cc\ub294 \ud6a8\uacfc \uce21\uba74\uc5d0\uc11c \uae30\uc874 \uce58\ub8cc\uc81c\ub4e4\uc744 \ub6f0\uc5b4\ub118\ub294 \uc131\uacfc\ub97c \ubcf4\uc774\uba70, SMA \uce58\ub8cc\uc758 \uc0c8\ub85c\uc6b4 \uae30\uc900\uc744 \uc81c\uc2dc\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>57\uac1c \uc5f0\uad6c\ub97c \ubd84\uc11d\ud55c \uba54\ud0c0\ubd84\uc11d \uacb0\uacfc\uc5d0 \ub530\ub974\uba74, \uc720\uc804\uc790 \uce58\ub8cc\ub294 95%\uc758 \uc0dd\uc874\uc728\uc744 \uae30\ub85d\ud588\uc73c\uba70, \uc778\uacf5\ud638\ud761 \ubcf4\uc870\uac00 \ud544\uc694\ud55c \ud658\uc790 \uc218\ub97c \uc720\uc758\ubbf8\ud558\uac8c \uac10\uc18c\uc2dc\ucf30\uc2b5\ub2c8\ub2e4. \ud2b9\ud788 \uc601\uc544 \ud658\uc790\uc5d0\uc11c \ub2e4\ub978 \uce58\ub8cc\ubc95\uacfc \ube44\uad50\ud574 \uc6b4\ub3d9 \uae30\ub2a5 \uac1c\uc120\uacfc \uc0dd\uc874\uc728 \ud5a5\uc0c1 \uce21\uba74\uc5d0\uc11c \ub354 \uc6b0\uc218\ud55c \ud6a8\uacfc\ub97c \ubcf4\uc600\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ub2e4\ub9cc \uc774\ub7ec\ud55c \uce58\ub8cc\ubc95, \ud2b9\ud788 \uc720\uc804\uc790 \uce58\ub8cc\ub294 \ubd81\ubbf8\uc640 \uc720\ub7fd\ucc98\ub7fc \ubcf4\ud5d8 \uae09\uc5ec \uc815\ucc45\uc774 \uc0c1\ub300\uc801\uc73c\ub85c \uc6b0\ud638\uc801\uc778 \uc9c0\uc5ed\uc5d0\uc11c \uc811\uadfc\uc131\uc774 \ud604\uc800\ud788 \ub192\uc740 \uac83\uc73c\ub85c \ub098\ud0c0\ub0ac\uc2b5\ub2c8\ub2e4.<\/p>\n<ul>\n<li>\n<h3><strong>\uc0ac\ud68c\uacbd\uc81c\uc801 \uc694\uc778: \uaca9\ucc28\ub97c \uc881\ud788\ub294 \uacfc\uc81c<\/strong><\/h3>\n<\/li>\n<\/ul>\n<p>\uc18c\ub4dd \uc218\uc900\uc740 SMA \uce58\ub8cc \uc811\uadfc\uc131\uc744 \uacb0\uc815\uc9d3\ub294 \ud575\uc2ec \uc694\uc778\uc73c\ub85c, \uace0\uc18c\ub4dd \uc9c0\uc5ed\uacfc \uc800\uc18c\ub4dd \uc9c0\uc5ed \uac04\uc5d0 \ub69c\ub837\ud55c \uaca9\ucc28\ub97c \ub9cc\ub4e4\uc5b4\ub0c5\ub2c8\ub2e4. \ubd80\uc720\ud55c \uad6d\uac00\uc5d0\uc11c\ub294 \uccb4\uacc4\uc801\uc73c\ub85c \uad6c\ucd95\ub41c \uc758\ub8cc \uc2dc\uc2a4\ud15c\uacfc \uad6d\uac00 \ub2e8\uc704 \ud658\uc790 \ub4f1\ub85d \uc2dc\uc2a4\ud15c\uc744 \ubc14\ud0d5\uc73c\ub85c \uc9c4\ub2e8\uc728\uc774 \ub192\uace0 SMA \uc804\ubb38 \uce58\ub8cc\uc5d0 \ub300\ud55c \uc811\uadfc\uc131\ub3c4 \uc0c1\ub300\uc801\uc73c\ub85c \uc6b0\uc218\ud569\ub2c8\ub2e4.<\/p>\n<p>\ubc18\uba74 \uc800\uc18c\ub4dd \uc9c0\uc5ed\uc5d0\uc11c\ub294 \uc758\ub8cc \uc7ac\uc815\uc758 \ud55c\uacc4, \uc2e0\uacbd\uadfc\uc721 \uc9c8\ud658 \uc804\ubb38\uc758 \ubd80\uc871, \uacfc\ub3c4\ud558\uac8c \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uc774 \uc911\ub300\ud55c \uc7a5\ubcbd\uc73c\ub85c \uc791\uc6a9\ud569\ub2c8\ub2e4. \ucda9\ubd84\ud55c \uc7ac\uc815\uc801 \uc9c0\uc6d0\uc774 \uc5c6\ub294 \uacbd\uc6b0, \ub9ce\uc740 \uac00\uc815\uc774 \uce58\ub8cc\ub97c \ubc1b\uae30 \uc704\ud574 \ud06c\ub77c\uc6b0\ub4dc\ud380\ub529\uacfc \uac19\uc740 \ub300\uccb4 \uc790\uae08 \uc870\ub2ec \ubc29\uc2dd\uc5d0 \uc758\uc874\ud560 \uc218\ubc16\uc5d0 \uc5c6\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774\ub7ec\ud55c \uacbd\uc81c\uc801 \uaca9\ucc28\ub294 SMA \uce58\ub8cc\uc758 \ud575\uc2ec\uc801\uc778 \uacfc\uc81c\ub97c \ub4dc\ub7ec\ub0c5\ub2c8\ub2e4. \ud658\uc790\uc758 \uc7ac\uc815\uc801 \uc5ec\uac74\uacfc \ubb34\uad00\ud558\uac8c, \uc801\uc2dc\uc5d0 \uc9c4\ub2e8\ubc1b\uace0 \ud6a8\uacfc\uc801\uc778 \uce58\ub8cc\uc5d0 \uc811\uadfc\ud560 \uc218 \uc788\ub294 \ud658\uacbd\uc744 \ub9c8\ub828\ud558\ub294 \uac83\uc774 \uc5ec\uc804\ud788 \uc911\uc694\ud55c \uacfc\uc81c\ub85c \ub0a8\uc544 \uc788\uc2b5\ub2c8\ub2e4..<\/p>\n<h3><strong>\ub2e4\uac01\uc801 \uc811\uadfc\uc758 \ud544\uc694\uc131<\/strong><\/h3>\n<p>\uc720\uc804\uc801 \uc694\uc778, \uc758\ub8cc \uc2dc\uc2a4\ud15c, \uc0ac\ud68c\uacbd\uc81c\uc801 \uc694\uc778\uc774 \uc11c\ub85c \ub9de\ubb3c\ub9ac\uba70 \ud615\uc131\ub418\ub294 \ubcf5\ud569\uc801\uc778 \ud658\uacbd\uc740 SMA \uc720\ubcd1\ub960\uc744 \uc774\ud574\ud558\uace0 \ub300\uc751\ud558\uae30 \uc704\ud574 \ub2e4\uac01\uc801\uc778 \uc811\uadfc\uc774 \ud544\uc694\ud568\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \ub300\ub9ac \uc778\uad6c(proxy population)\uc640 \uce58\ub8cc \uc811\uadfc\uc131\uae4c\uc9c0 \ud568\uaed8 \uace0\ub824\ud568\uc73c\ub85c\uc368, SMA\uac00 \uc804 \uc138\uacc4\uc5d0 \ubbf8\uce58\ub294 \uc601\ud5a5\uc744 \ubcf4\ub2e4 \uc785\uccb4\uc801\uc73c\ub85c \uc774\ud574\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ub530\ub77c\uc11c \uc55e\uc73c\ub85c SMA\uc5d0 \ub300\ud574 \uc774\uc57c\uae30\ud560 \ub54c, \uc774\ub97c \ub2e8\uc21c\ud55c \uc720\uc804 \uc9c8\ud658\uc73c\ub85c\ub9cc \ubc14\ub77c\ubcf4\uae30\ubcf4\ub2e4\ub294 \ub2e4\uc591\ud55c \uc694\uc778\uc774 \uc5bd\ud600 \ud615\uc131\ub41c \uae00\ub85c\ubc8c \ud37c\uc990\uc774\ub77c\ub294 \uc810\uc744 \ud568\uaed8 \ub5a0\uc62c\ub9b4 \ud544\uc694\uac00 \uc788\uc2b5\ub2c8\ub2e4. \uc9c0\uc18d\uc801\uc778 \uc5f0\uad6c\uc640 \ud611\uc5c5\uc744 \ud1b5\ud574 \uc720\uc804\ud559, \uacbd\uc81c\uc801 \ud658\uacbd, \uc758\ub8cc \uc811\uadfc\uc131\uc774 SMA \uc720\ubcd1\ub960\uc5d0 \uc5b4\ub5a4 \uc601\ud5a5\uc744 \ubbf8\uce58\ub294\uc9c0 \ub354 \uae4a\uc774 \uc774\ud574\ud558\uace0, \uc774 \uc5b4\ub824\uc6b4 \uc9c8\ud658\uc73c\ub85c \uc601\ud5a5\uc744 \ubc1b\ub294 \ud658\uc790\ub4e4\uc758 \uc0b6\uc744 \uac1c\uc120\ud574 \ub098\uac08 \uc218 \uc788\uc744 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\ud074\ub798\ub9ac\ubca0\uc774\ud2b8\uac00 \uc0b0\uc5c5 \ud45c\uc900 \uc5ed\ud559 \uc778\ud154\ub9ac\uc804\uc2a4\ub97c \ud65c\uc6a9\ud574 \uc0dd\uba85\uacfc\ud559 \uae30\uc5c5\uc758 \uc2dc\uc7a5 \uaddc\ubaa8 \uc0b0\uc815\uc744 \uc5b4\ub5bb\uac8c \uc9c0\uc6d0\ud558\ub294\uc9c0\uc5d0 \ub300\ud574 \ub354 \uc54c\uc544\ubcf4\uc2dc\ub824\uba74 \ub2e4\uc74c \ub9c1\ud06c\ub97c \ucc38\uace0\ud574 \uc8fc\uc138\uc694. <a href=\"https:\/\/clarivate.com\/life-sciences-healthcare\/ko\/portfolio-strategy\/market-assessment\/epidemiology-intelligence\/\">\uc5ed\ud559 \uc778\ud154\ub9ac\uc804\uc2a4 \u2013 Epidemiology Intelligence | \ud074\ub798\ub9ac\ubca0\uc774\ud2b8<\/a><\/p>\n<p><em>\ubcf8 \ube14\ub85c\uadf8 \uae00\uc740 Alex Li, MD, PhD (\uc218\uc11d \uc5ed\ud559 \uc804\ubb38\uac00)\uc640 Shyama Ghosh, PhD (STEM\ucf58\ud150\uce20 \ubd84\uc57c \uc218\uc11d \ubd84\uc11d\uac00)\uac00 \uacf5\ub3d9 \uc9d1\ud544\ud588\uc2b5\ub2c8\ub2e4.<\/em><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ucc99\uc218\uc131\uadfc\uc704\ucd95\uc99d(Spinal Muscular Atrophy, SMA)\uc740 \ucc99\uc218 \ub0b4 \uc54c\ud30c \uc6b4\ub3d9\uc2e0\uacbd\uc138\ud3ec\uac00 \uc810\uc9c4\uc801\uc73c\ub85c \uc190\uc0c1\ub418\uba74\uc11c \uadfc\uc721 \uc57d\ud654\uc640 \uc704\ucd95\uc774 \uc9c4\ud589\ub418\ub294 \ud76c\uadc0 \uc720\uc804 \uc9c8\ud658\uc785\ub2c8\ub2e4. \ubcf8 \ube14\ub85c\uadf8 \uae00\uc740 \uc5ec\ub7ec \uc9c0\uc5ed\uc5d0\uc11c \uc218\uc9d1\ud55c \uc720\ubcd1\ub960 \ub370\uc774\ud130\ub97c \ubc14\ud0d5\uc73c\ub85c \uc218\ud589\ud55c \uad11\ubc94\uc704\ud55c \uc5ed\ud559 \ubd84\uc11d\uc744&#8230;<\/p>\n","protected":false},"author":59,"featured_media":10164,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"_links_to":"","_links_to_type":0,"footnotes":""},"categories":[2452],"tags":[2565,2591,2627,2630,2633,1404],"class_list":["post-573635","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-biopharma","tag-business-development","tag-epidemiology","tag-market-access-2","tag-neuroscience","tag-rd","tag-rare-disease"],"acf":[],"lang":"ko","translations":{"ko":573635,"en":571602,"ja":572725},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"pll_sync_post":[],"_links":{"self":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts\/573635","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/users\/59"}],"replies":[{"embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/comments?post=573635"}],"version-history":[{"count":3,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts\/573635\/revisions"}],"predecessor-version":[{"id":573638,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts\/573635\/revisions\/573638"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/media\/10164"}],"wp:attachment":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/media?parent=573635"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/categories?post=573635"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/tags?post=573635"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}