{"id":12578,"date":"2023-05-24T17:48:33","date_gmt":"2023-05-24T08:48:33","guid":{"rendered":"https:\/\/clarivate.com\/ko\/?p=12578"},"modified":"2024-11-06T02:57:08","modified_gmt":"2024-11-06T02:57:08","slug":"gene-therapies-transform-rare-disease-treatment-hope-for-patients-amidst-regulatory-payer-and-developer-challenges","status":"publish","type":"post","link":"https:\/\/clarivate.com\/life-sciences-healthcare\/ko\/blog\/gene-therapies-transform-rare-disease-treatment-hope-for-patients-amidst-regulatory-payer-and-developer-challenges\/","title":{"rendered":"\uc720\uc804\uc790 \uce58\ub8cc\uc81c, \ud76c\uadc0\uc9c8\ud658\uc758 \uce58\ub8cc\ub97c \ubcc0\ud654\uc2dc\ud0a4\ub2e4: \uaddc\uc81c, \uc9c0\ubd88\uc790 \ubc0f \uac1c\ubc1c\uc790\ub4e4\uc774 \ub9c8\uc8fc\ud55c \uacfc\uc81c\ub4e4\uacfc \ud658\uc790\ub97c \uc704\ud55c \ud76c\ub9dd"},"content":{"rendered":"<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-12579\" src=\"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-content\/uploads\/sites\/4\/2023\/05\/matthew-arnold_avatar-140x140-1.jpg\" alt=\"\" width=\"140\" height=\"140\" srcset=\"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-content\/uploads\/sites\/4\/2023\/05\/matthew-arnold_avatar-140x140-1.jpg 140w, https:\/\/clarivate.com\/life-sciences-healthcare\/wp-content\/uploads\/sites\/4\/2023\/05\/matthew-arnold_avatar-140x140-1-40x40.jpg 40w\" sizes=\"auto, (max-width: 140px) 100vw, 140px\" \/><\/p>\n<p>MATTHEW ARNOLD<\/p>\n<p><strong>\uc218\uc11d\ubd84\uc11d\uac00, \ud074\ub798\ub9ac\ubca0\uc774\ud2b8<\/strong><\/p>\n<p>&nbsp;<\/p>\n<p><em>FDA AdComm\uc774 \ucd5c\uadfc\uc5d0 \uc218\ud589\ud55c Sarepta\uc758 \uc0c8\ub85c\uc6b4 \uc720\uc804\uc790 \uc804\ub2ec \uce58\ub8cc\uc81c\uc640 \uad00\ub828\ub41c \uac00\uc18d\uc2b9\uc778 \ud22c\ud45c\ub294 \ud76c\uadc0\ubcd1 \uce58\ub8cc\ub97c \uc704\ud55c \ud601\uc2e0\uc801\uc778 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\ub4e4\uc774 \uc2dc\uc7a5\uc5d0 \ub3c4\ucc29\ud568\uc5d0 \ub530\ub77c \uaddc\uc81c\uae30\uad00, \uc9c0\ubd88\uc790 \ubc0f \uac1c\ubc1c\uc790\uac00 \uc9c1\uba74\ud55c \uc5ec\ub7ec \ubb38\uc81c\ub97c \ubcf4\uc5ec\uc90d\ub2c8\ub2e4.<\/em><\/p>\n<p>\ub4a4\uc2dc\uc5d4\ub290 \uadfc\uc774\uc601\uc591\uc99d(DMD)\ud658\uc790\uc640 \uac04\ubcd1\uc778\ub4e4\uc740 <a href=\"https:\/\/www.bioworld.com\/articles\/696971-sareptas-dmd-gene-therapy-squeaks-past-adcom-with-8-6-vote\" target=\"_blank\" rel=\"noopener\">\ubbf8\uad6d FDA \uc790\ubb38\uc704\uc6d0\ud68c\uac00 \uc720\uc804\uc790 \uc804\ub2ec \uc694\ubc95\uc744 \ud65c\uc6a9\ud55c \uc2e0\uc57d\uc5d0 \ub300\ud55c \uac00\uc18d\uc2b9\uc778\uc744 \ucd94\ucc9c\ud558\ub294\ub370 \uad00\ud55c \ud45c\uacb0\uc774 \ucc2c\uc131 8 \ubc18\ub300 6\uc73c\ub85c \ud1b5\uacfc\ud55c \uac83\uc5d0<\/a> \ub300\ud574 \ud658\uc601\ud558\ub294 \ubaa8\uc2b5\uc744 \ubcf4\uc600\uc2b5\ub2c8\ub2e4. \ubcf8 \ud22c\ud45c\ub294 \uaddc\uc81c\uae30\uad00\uc774 \uc2dc\uacc4\uc5f4 \ub370\uc774\ud130\uac00 \uc5c6\ub294 \ud76c\uadc0\ubcd1\uc744 \uc704\ud55c \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95\uc744 \ud3c9\uac00\ud558\ub294 \ubc29\ubc95\uc5d0 \ub300\ud574 \uace0\ubbfc\ud558\uace0 \uc788\uc74c\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4.<\/p>\n<p>\ud074\ub798\ub9ac\ubca0\uc774\ud2b8\uc758 \uac10\uc5fc\uc131, \ud2c8\uc0c8 \ubc0f \ud76c\uadc0\ubcd1\uc5d0 \ub300\ud55c \uc758\ub8cc \uc5f0\uad6c \ubd84\uc11d \ucc45\uc784\uc790\uc778 Bethany Kiernan\ub294 \u201c\ucd5c\uadfc \uba87 \ub144 \ub3d9\uc548 FDA\ub294 \uce58\ub8cc\uc81c \uc2b9\uc778\uc744 \uc704\ud55c \uadfc\uac70\ub85c \ub300\ub9ac\uc9c0\ud45c\uc744 \ud65c\uc6a9\ud558\ub294 \uac83\uc744 \uc810\ucc28\uc801\uc73c\ub85c \ud5c8\uc6a9\ud558\ub294 \ubaa8\uc2b5\uc744 \ubcf4\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4.\u201d\ub77c\uba74\uc11c \u201c\ube44\ub85d \uc555\ub3c4\uc801 \uc758\uacac\uc740 \uc544\ub2c8\uc5c8\uc9c0\ub9cc, \ub300\ub9ac\uc9c0\ud45c\ub97c \ud1b5\ud574 \uc5bb\uc740 \ud6a8\ub2a5 \ub370\uc774\ud130\uac00 Sarepta\uc758 \uc2e0\uc57d\uc744 \uac00\uc18d\uc2b9\uc778\uc744 \ud558\uae30\uc5d0 \ucda9\ubd84\ud558\ub2e4\uace0 \ub9d0\ud55c \uc704\uc6d0\ud68c\uc758 \ub9d0\uc740 \ub9e4\uc6b0 \ud765\ubbf8\ub85c\uc6b8 \ubfd0 \uc544\ub2c8\ub77c \uae0d\uc815\uc801\uc785\ub2c8\ub2e4. \ud2b9\ud788, \uadfc\uc704\ucd95\uc99d\uacfc \uac19\uc740 \uc9c8\ud658\uc5d0\ub294 \uc5ec\uc804\ud788 \uc218\ub9ce\uc740 \ucda9\uc871\ub418\uc9c0 \uc54a\uc740 \uc694\uad6c\ub4e4\uc774 \uc788\uc2b5\ub2c8\ub2e4.\u201d<\/p>\n<p>\ud55c\ud3b8, \uc9c0\ubd88\uc790\ub4e4\uc5d0\uac8c Sarepta Therapeutics\uc758 SRP-9001\uc5d0 \ub300\ud55c \ud22c\ud45c\uacb0\uacfc\ub294 \uac00\uce58\ud3c9\uac00\uc640 \uc774\uc6a9\uad00\ub9ac \uc2e4\ucc9c\uacfc\uc81c\uac00 \uae34\uae09\ud788 \ub2e4\ub8e8\uc5b4\uc838\uc57c \ud568\uc744 \uc2dc\uc0ac\ud569\ub2c8\ub2e4. \ud074\ub798\ub9ac\ubca0\uc774\ud2b8\ub294 \ucd5c\uadfc \ubcf4\uace0\uc11c\u00a0<a href=\"https:\/\/clarivate.com\/lp\/five-key-trends-in-gene-therapy-approvals-and-access\/\"><em>\uc720\uc804\uc790 \uce58\ub8cc\uc81c \uc2b9\uc778 \ubc0f \uc561\uc138\uc2a4\uc5d0 \uad00\ud55c <\/em><em>5\uac00\uc9c0 \uc8fc\uc694 \ud2b8\ub80c\ub4dc<\/em><\/a><em><u>\ub97c \ud1b5\ud574 <\/u><\/em>\u00a0\u00a0\ubbf8\uad6d\uc758 \uc9c0\ubd88\uc790\ub4e4\uc740 \uac74\uac15 \uacbd\uc81c\ud559 \uacb0\uacfc \uc5f0\uad6c\ub97c \uc810\ucc28\uc801\uc73c\ub85c \uc758\uc0ac\uacb0\uc815\uc5d0 \ud1b5\ud569\ud558\uace0, \uc81c\uc870\uc5c5\uccb4\uc640 \uacb0\uacfc \uc911\uc2ec\uc758 \uacc4\uc57d\uc744 \ub9fa\uace0 \uc788\ub2e4\uace0 \ubc1d\ud614\uc2b5\ub2c8\ub2e4. \uc774 \ubfd0 \uc544\ub2c8\ub77c, DMD\uce58\ub8cc\uc81c\uc758 \uacbd\uc6b0 \ub2e8\uc77c \uce58\ub8cc\uc640 \ub9cc\uc131 \uce58\ub8cc\uc758 \uac00\uce58\uac00 \ub17c\uc758\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>Sarepta\uc758 \uc774\uc804 DMD\ud658\uc790\uc6a9 \uc758\uc57d\ud488\uc778EXONDYS 51(antisense oligonucleotide (ASO))\uc774 2016\ub144 FDA\uc2b9\uc778\uc744 \ubc1b\uc558\uc744 \ub54c, \uc774 \uc81c\ud488\uc740 \ud658\uc790 \ub2f9 \uc5f0\ud3c9\uade0 \u00a0<a href=\"https:\/\/www.statnews.com\/pharmalot\/2016\/09\/19\/sarepta-duchenne-drug-prices\" target=\"_blank\" rel=\"noopener\">3\ub9cc\ub2ec\ub7ec\ub85c \uac00\uaca9\uc774 \ucc45\uc815\ub418\uc5c8\uc2b5\ub2c8\ub2e4. <\/a>\uadfc\uc721 \ud1f4\ud654 \uc9c8\ud658\uc778 \uc774 \uce58\uba85\uc801\uc778 \ud76c\uadc0\ubcd1\uc740 \uc804 \uc138\uacc4\uc801 \uc57d 3\ucc9c 5\ubc31\uba85~ 5\ucc9c\uba85\uc758 \uc2e0\uc0dd\ub0a8\uc544 \uc911 \ud55c \uba85\uc5d0\uac8c \ubc1c\ubcd1\ub418\uba70, \uccab \uc99d\uc0c1\uc774 \ub300\ubd80\ubd84 \uc601\uc720\uc544 \ub54c \ubc1c\ud604\ub418\uace0 \ub300\ubd80\ubd84\uc758 \uacbd\uc6b0, \uc774 \uc9c8\ud658 \ud658\uc790\ub4e4\uc774 10\ub300\uac00 \ub418\uae30 \uc804 \ud720\uccb4\uc5b4\ub97c \uc0ac\uc6a9\ud558\uac8c \ub429\ub2c8\ub2e4.<\/p>\n<h3><strong>\ucda9\uc871\ub418\uc9c0 \uc54a\uc740 \uc218\uc694 <\/strong><strong>VS \ube44\uc6a9<\/strong><\/h3>\n<p>Sarepta\uac00 \ub0b4\ub193\uc740 EXONDYS 51\uac00\uaca9\uc5d0 \uc6d4\uc2a4\ud2b8\ub9ac\ud2b8\ub294 \ub180\ub77c\uc6c0\uc744 \ud45c\uba85\ud588\uc2b5\ub2c8\ub2e4. \uc560\ub110\ub9ac\uc2a4\ud2b8\ub4e4\uc740 \uc774 \uc8fc\uc0ac\uc81c\uac00 \ub354 \uace0\uac00\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ud588\uae30 \ub54c\ubb38\uc785\ub2c8\ub2e4. 11\uac1c\uc758 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uac00 \uc774\ubbf8 \uc2b9\uc778\uc744 \ubc1b\uc558\uace0, Cortellis Competitive Intelligence\u2122 \ub370\uc774\ud130\uc5d0 \ub530\ub974\uba74 \ub610 \ub2e4\ub978 30\uac1c\uc758 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uac00 \ud6c4\uae30 \ub2e8\uacc4\uc758 \ud30c\uc774\ud504\ub77c\uc778\uc5d0 \uc788\uc74c\uc744 \ud655\uc778\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4. \uc9c0\ubd88\uc790\ub4e4\uc740 \uc774\uc640 \uad00\ub828\ub41c \uc601\ud5a5\uc744 \uc608\uce21\ud558\ub294 \ud55c\ud3b8 \ub300\ube44\ud558\ub294 \ubaa8\uc2b5\uc744 \ubcf4\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>SRP-9001\uc740 EXONDYS 51 \ubc0f Sarepta\uc758 \ub2e4\ub978ASO\uc640\ub294 \ub2ec\ub9ac \uadfc\uc721\ub2e8\ubc31\uc9c8 \uc720\uc804\uc790\uc778 \ub514\uc2a4\ud2b8\ub85c\ud540 \uc720\uc804\uc790\uc758 \ud2b9\uc815 \ub3cc\uc5f0\ubcc0\uc774\ub97c \ub300\uc0c1\uc73c\ub85c \ud558\uc9c0 \uc54a\uace0,\ubc18\ubcf5\uc801\uc778 \uce58\ub8cc\ub3c4 \ud544\uc694\ud558\uc9c0 \uc54a\uc2b5\ub2c8\ub2e4. SRP-9001\uc740 \ubcf4\ub2e4 \ub113\uc740 \ubc94\uc704\uc758 \ub3cc\uc5f0\ubcc0\uc774\ub97c \uac00\uc9c4 \ud658\uc790\uc5d0\uac8c \ub2e8\uc77c \ud22c\uc5ec \uc694\ubc95\uc73c\ub85c \uc0ac\uc6a9 \uac00\ub2a5\ud569\ub2c8\ub2e4. \ub610\ud55c, \ud604\uc7ac \ubcf4\ud589\uc774 \uac00\ub2a5\ud55c \uc77c\ubc18\uc801\uc73c\ub85c 10\ub300 \uc804\ubc18\uae30\uc5d0 \ud574\ub2f9\ud558\ub294 \uadfc\uae30\ub2a5\uc758 \ud070 \uc190\uc2e4\uc774 \uc5c6\ub294 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \ud14c\uc2a4\ud2b8 \uc911\uc785\ub2c8\ub2e4. \ud074\ub798\ub9ac\ubca0\uc774\ud2b8\uc5d0\uc11c\ub294 2022\ub144 3\uc6d4\u00a0<a href=\"https:\/\/clarivate.com\/products\/research-reports\/disease-landscape-and-forecast\/access-reimbursement\/\">Access &amp; Reimbursement \ubcf4\uace0\uc11c<\/a>\ub97c \ud1b5\ud574 \ub9ce\uc740Managed Care Organization \uc784\uc6d0\ub4e4\uc774 \uc774\ub7f0 \uc2e0\uc0dd DMD\uce58\ub8cc\ubc95\uc744 \ubcf4\uc7a5\ud560\uc9c0\ub294 \uc5ec\uc804\ud788 \ubd88\ud655\uc2e4\ud558\uba70, \ud658\uc790\ub4e4\uc758 \uc811\uadfc\uc131 \ud655\ubcf4\uc5d0 \uc788\uc5b4 Real World Data\ub97c \uc218\uc9d1\ud558\ub294 \uac83\uc774 \ub9e4\uc6b0 \uc911\uc694\ud558\ub2e4\uace0 \ubc1d\ud614\uc2b5\ub2c8\ub2e4. \uc9c0\ubd88\uc790\ub4e4\uc740 \ud604\uc7ac, \ubd88\ud544\uc694\ud55c \uce58\ub8cc\ub97c \uc608\ubc29\ud558\uace0 \ube44\uc6a9\uc744 \ud1b5\uc81c\ud558\uae30 \uc704\ud574 \ub2e4\uc591\ud558\uace0\ub3c4 \uc5c4\uaca9\ud55c \uc774\uc6a9 \uad00\ub9ac \uc870\uce58\ub97c \uace0\ub824 \uc911\uc785\ub2c8\ub2e4.<\/p>\n<p>Bethany Kiernan \uc740 \u201c\uc9c0\ubd88\uc790\ub4e4\uc740 \uc720\uc804\uc790 \uce58\ub8cc\ub97c \ud3ec\ud568\ud55c \ud2b9\uc218 \uce58\ub8cc\uc5d0 \ub300\ud55c \ube44\uc6a9 \ubd80\ub2f4\ub54c\ubb38\uc5d0 \ud658\uc790\uac00 \uce58\ub8cc \uae30\uc900\uc744 \ucda9\uc871\ud558\ub294 \uc9c0\uc5d0 \ub300\ud55c \uc5ec\ubd80\ub97c \ub9e4\uc6b0 \uc5c4\uaca9\ud558\uac8c \ud655\uc778\ud560 \uac83\uc785\ub2c8\ub2e4. \ud558\uc9c0\ub9cc DMD\ub294 \uc720\uc804\uc801 \uc9c8\ud658\uc774\uace0 \uba85\ud655\ud55c \uc9c4\ub2e8\uc774 \uc788\uae30 \ub54c\ubb38\uc5d0 \uc774\ub7f0 \uacfc\uc815\uc774 \ud658\uc790\uc640 \uc758\uc0ac\ub4e4\uc5d0\uac8c \uc0c1\ub300\uc801\uc73c\ub85c \uac04\ub2e8\ud55c \uacfc\uc815\uc774 \ub420 \uac83\uc774\ub77c\ub294 \ud76c\ub9dd\uc774 \uc788\uae30\ub3c4 \ud569\ub2c8\ub2e4.\u201d\uace0 \ub9d0\ud569\ub2c8\ub2e4.<\/p>\n<p>Access&amp; Reimbursement\uc5f0\uad6c \ubcf4\uace0\uc11c\uc5d0\uc11c \uac15\uc870\ud588\ub4ef, \uc0ac\uc804 \uc2b9\uc778\uc740 \ucc28\uc138\ub300 DMD \uc720\uc804\uc790 \uce58\ub8cc\ubc95 \ucc98\ubc29 \uc2dc, \uc2e0\uacbd\uacfc \uc758\uc0ac\ub4e4\uc758 \uac00\uc7a5 \ud070 \uac71\uc815\uac70\ub9ac \uc911 \ud558\ub098\uc785\ub2c8\ub2e4. \uc2e0\uacbd\uacfc \uc758\uc0ac\ub4e4\uc740 \uacfc\ub3c4\ud55c \ubcf8\uc778\ubd80\ub2f4 \ube44\uc6a9, \uac00\uc7a5 \uc2ec\uac01\ud55c \uc99d\ub840\uc5d0 \ub300\ud55c \uc81c\ud55c \ubc0f \uc7ac \uc778\uc99d \ub4f1\uc744 \uadf8 \ub2e4\uc74c\uc758 \uac71\uc815\uac70\ub9ac\ub85c \uaf3d\uc558\uc2b5\ub2c8\ub2e4. \uc9c8\ubcd1\uc758 \uc9c4\ud589\uc801\uc778 \ud2b9\uc131\uc744 \uace0\ub824\ud558\uba74, \uc774\ub7f0 DMD\uce58\ub8cc\ubc95\uc774 \uc2dc\ud310 \uc2b9\uc778\uc744 \ubc1b\uac8c \ub420 \uacbd\uc6b0, \uce58\ub8cc\uae4c\uc9c0 \uac78\ub9ac\ub294 \uc2dc\uac04\uc774 \ub9e4\uc6b0 \uc911\uc694\ud574 \uc9c8 \uac83\uc785\ub2c8\ub2e4. (Pfizer\uc640Solid Biosciences\ub3c4 \ud6c4\uae30 \ub2e8\uacc4\uc758 \ud6c4\ubcf4\ubb3c\uc9c8\uc744 \uac1c\ubc1c\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.)<\/p>\n<p>Bethany Kiernan \uc740 \u201c\uadfc\uc721 \uc774\uc601\uc591\uc99d\uc5d0 \ub300\ud55c \uc720\uc804 \uac80\uc0ac \ubc0f \uae30\ud0c0 \ud655\ub9bd\ub41c \uc9c4\ub2e8 \uac80\uc0ac\uac00 \uc788\uc5b4, \uc5b4\ub9b0\uc774\ub4e4\uc774 \uc870\uae30\uc5d0 \ubcd1\uc744 \uc9c4\ub2e8\ubc1b\ub294 \uacbd\uc6b0\uac00 \ub9ce\uc2b5\ub2c8\ub2e4.\u201d\ub77c\uba74\uc11c \u201c\uadfc\uc721 \uc774\uc601\uc591\uc99d \ud611\ud68c\uc640 \ubd80\ubaa8\ub4e4\uc740 \ub9e4\uc6b0 \ud65c\ubc1c\ud558\uac8c \ud65c\ub3d9\ud558\uace0 \uc788\uc73c\uba70, \uce58\ub8cc\uc81c \uc811\uadfc\uc744 \uc704\ud574 \uc2b9\uc778\uc744 \ucd5c\ub300\ud55c \ube60\ub974\uac8c \ud558\ub824\ub294 \ub178\ub825\uc744 \ud589\ud560 \uac83\uc774\ub77c \uc608\uc0c1\ud569\ub2c8\ub2e4.\u201d\uace0 \ub9d0\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc9c0\ubd88\uc790, \uaddc\uc81c\uae30\uad00, \uc81c\uc57d\ubc14\uc774\uc624\ud68c\uc0ac\ub4e4\uc774 \uc548\uc804\ud558\uace0 \ud6a8\uacfc\uc801\uc73c\ub85c \uc720\uc804\uc790 \uce58\ub8cc\uc81c\ub97c \ud658\uc790\uc5d0\uac8c \uc804\ub2ec\ud558\uae30 \uc704\ud574 \uc9c1\uba74\ud558\uace0 \uc788\ub294 \ub3c4\uc804\uacfc\uc81c\ub4e4\uc5d0 \ub300\ud574 \ubcf4\ub2e4 \uc790\uc138\ud788 \uc54c\uace0 \uc2f6\uc73c\uc2e0 \ubd84\ub4e4\uc740 \ud074\ub798\ub9ac\ubca0\uc774\ud2b8\uc758 \uc0c8\ub85c\uc6b4 \ubcf4\uace0\uc11c\uc778 \u00a0<a href=\"https:\/\/clarivate.com\/lp\/five-key-trends-in-gene-therapy-approvals-and-access\/\"><em>\uc720\uc804\uc790 \uce58\ub8cc\uc81c \uc2b9\uc778 \ubc0f \uc561\uc138\uc2a4\uc5d0 \uad00\ud55c <\/em><em>5\uac00\uc9c0 \uc8fc\uc694 \ud2b8\ub80c\ub4dc<\/em><\/a> \ubcf4\uace0\uc11c\ub97c \ub2e4\uc6b4\ub85c\ub4dc \ud574 \ud655\uc778\ud574\uc8fc\uc2ed\uc2dc\uc624.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>MATTHEW ARNOLD \uc218\uc11d\ubd84\uc11d\uac00, \ud074\ub798\ub9ac\ubca0\uc774\ud2b8 &nbsp; FDA AdComm\uc774 \ucd5c\uadfc\uc5d0 \uc218\ud589\ud55c Sarepta\uc758 \uc0c8\ub85c\uc6b4 \uc720\uc804\uc790 \uc804\ub2ec \uce58\ub8cc\uc81c\uc640 \uad00\ub828\ub41c \uac00\uc18d\uc2b9\uc778 \ud22c\ud45c\ub294 \ud76c\uadc0\ubcd1 \uce58\ub8cc\ub97c \uc704\ud55c \ud601\uc2e0\uc801\uc778 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\ub4e4\uc774 \uc2dc\uc7a5\uc5d0 \ub3c4\ucc29\ud568\uc5d0 \ub530\ub77c \uaddc\uc81c\uae30\uad00, \uc9c0\ubd88\uc790 \ubc0f \uac1c\ubc1c\uc790\uac00&#8230;<\/p>\n","protected":false},"author":207,"featured_media":12580,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"_links_to":"","_links_to_type":0,"footnotes":""},"categories":[1315],"tags":[2007,1404],"class_list":["post-12578","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-life-sciences-healthcare","tag-researchcommercialization","tag-rare-disease","clarivate-industry-life-sciences-and-healthcare","clarivate-product-biopharma"],"acf":[],"lang":"ko","translations":{"ko":12578,"en":220028},"publishpress_future_workflow_manual_trigger":{"enabledWorkflows":[]},"pll_sync_post":[],"_links":{"self":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts\/12578","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/users\/207"}],"replies":[{"embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/comments?post=12578"}],"version-history":[{"count":1,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts\/12578\/revisions"}],"predecessor-version":[{"id":310625,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/posts\/12578\/revisions\/310625"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/media\/12580"}],"wp:attachment":[{"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/media?parent=12578"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/categories?post=12578"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/clarivate.com\/life-sciences-healthcare\/wp-json\/wp\/v2\/tags?post=12578"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}